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A new class
of gene therapy.
We’re pushing the limits of genetic medicine.
And our goal is no limits.
Spaces
matter.
See our
liver disease programs.
Therapeutic Reach
Fuller Lives.
Discover
ceDNA.
Redosable
A new
reality.
Discover
ctLNP.
Global Potential
Scalable
manufacturing.
See our retina
disease program.
Meet Penny
and Simon.
Capsid-free
manufacturing.
Broad Therapeutic Reach.
Let’s hear it for fuller lives and fewer doctor appointments.
Delve into the possibilities unlocked by our closed-ended DNA.
REDOSABLE. TITRATABLE.
We see a new reality in genetic medicine ahead.
Focused on leaving nobody behind.
Our non-viral delivery can target specific cells while treating more people.
GLOBAL POTENTIAL.
If you can drastically improve lives, you won’t want to stop at a few thousand.
See the unlimited potential of our capsid-free manufacturing.
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