Zac and Jonathan: A brothers’ journeyby SARA DEN BESTEN, HEAD OF HUMAN RESOURCES
and Levi Gershkowitz, Living in the Light
"What motivated us to adopt was recognizing the need. There were kids everywhere who needed a mommy and daddy and we could do that.” — Paul Read More 
Penny and Simon take on the worldby SARA DEN BESTEN, HEAD OF HUMAN RESOURCES
and Levi Gershkowitz, Living in the Light
"There is no normal. There is only life." — Danny Penny and Simon aren’t your typical brother and sister.
Born from parents Danny and Jaime, who share a profound sense of wanderlust, they are already globe-hopping travelers, who have explored 12th century churches and uncovered Read More 
Manufacturing a global revolution in gene therapyby MARK ANGELINO, PhD, FOUNDER & CHIEF OPERATING OFFICER and GEOFF MCDONOUGH, MD, PRESIDENT & CHIEF EXECUTIVE OFFICER
In the early 1940s, Pfizer executive John Smith wrote of the revolutionary drug penicillin: “[T]he yields are low, the isolation is difficult, the extraction is murder, the purification invites disaster, and the assay is unsatisfactory.”1 Read More 
Moving forward: How our new space powers our mission to bring next generation gene therapies to patientsby SARA DEN BESTEN, HEAD OF HUMAN RESOURCES
and PAT MAROLDA, VP OF FACILITIES OPERATIONS AND EH&S
Although we do affectionately refer to it as “301,” our new headquarters is more than an address. It’s an integral part of who we are, what we value, and what we aim to achieve.
We are dedicated to fostering a culture where everyone Read More 
Bringing the light of gene therapy to more patientsby GEOFF MCDONOUGH, MD, PRESIDENT & CHIEF EXECUTIVE OFFICER
and DOUG KERR, MD, PhD, MBA, CHIEF DEVELOPMENT OFFICER
Thomas Edison’s first lightbulb in 1879 sparked a revolution. Using electricity that was passed through a platinum filament, his glass bulb required less power than the existing lamps of the day.
But it also lasted only a few hours before burning out. Read More 
Genetic diseases steal too many kids' futures. It doesn’t have to be this way.by GEOFF MCDONOUGH, MD, President & Chief Executive Officer and DOUG KERR, MD, PhD, MBA, Chief Development Officer
This piece was originally published on WBUR’s Cognoscenti.
I want to live in a world where children have never heard of hemophilia or cystic fibrosis, because we have all but eradicated those diseases.
This isn’t a dream. The biotech industry is beginning Read More 
Right from the beginning: returning to the origins of the orphan drug movementby GEOFF MCDONOUGH, MD, PRESIDENT & CHIEF EXECUTIVE OFFICER
This article was originally published as part of the From The Trenches feature of LifeSciVC.
Our industry stands at the beginning of the most significant opportunity to impact genetic and metabolic disease we have ever encountered – the ability to decisively intervene in the perinatal period with therapies capable of lifelong Read More 
